NHS Approves Revolutionary CRISPR Gene Therapy for Sickle Cell Disease

NHS Approves Revolutionary CRISPR Gene Therapy for Sickle Cell Disease In a landmark decision, the National Health Service (NHS) in England has approved the use of Casgevy, a groundbreaking CRISPR-based gene therapy, for patients aged 12 and older suffering from sickle cell disease (SCD) with recurrent vaso-occlusive crises. This approval marks a significant advancement in […]
Our first Short-Term Scientific Mission on Standardizing Annotation of Structural Hemoglobinopathies!

In March 2023, the first HELIOS-funded Short-Term Scientific Mission (STSM) was completed. The project was carried out by HELIOS member Maria Xenophontos from the Cyprus Institute of Neurology, in collaboration with Prof. Celeste Bento at the University Hospital Coimbra in Portugal. Maria spent two weeks working with Prof. Bento on a project titled “Enhancing Structural […]
HELIOS website goes live!

WG5 – Dissemination and outreach has just published the HELIOS website that you can visit here!